UK becomes the first country in the world to approve CRISPR gene editing therapy

The British drug regulatory agency MHRA (Medicines and Healthcare Products Regulatory Agency) announced on its official website that it has approved the CRISPR gene editing therapy Casgevy (exa-cel).



British regulators stated that this is the world's first gene editing therapy approved to treat this indication, and also the world's first approved therapy using the "gene scissors" CRISPR. This also marks that this breakthrough technology has become a practical treatment only 11 years after it first appeared in 2012.

It is worth mentioning that Emmanuelle Charpentier, who jointly won the Nobel Prize in Chemistry for this breakthrough technology in 2020, is one of the co-founders of CRISPR Therapeutics.

UK Greenlight

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